Press
- Media / Reuters 08.19.2022
- Press Release / GlobeNewswire 07.07.2022
- Press Release / Business Wire 10.20.2021
- Presentation / National Organization for Rare Disorders (NORD) 07.02.2021
- Media / NIH – Intramural Research Program Blog 02.10.2021
- Media / NIH Director’s Blog 01.02.2021
- Media / Pharma Times 12.24.2020
- Press Release / Business Wire 12.22.2020
- Media / BioPharma Dive 12.22.2020
- Media / Endpoints News 12.22.2020
- Media / FiercePharma 12.22.2020
- Media / FDA 12.21.2020
- Press Release / Business Wire 08.28.2020
- Press Release / Business Wire 07.29.2020
- Media / New York Times 08.12.2019